Orphan products: hope for people with rare diseases.

From: FDA Consumer | Date: November 1, 2003| Author: Rados, Carol | Copyright information

Jumping Frenchmen of Maine sounds like an uproarious, modern-day stage show or even a new wave rock group. But it's neither. It's the name of an unusual disorder that causes an extreme startle reaction to unexpected noises or sights. Though little is known about Jumping Frenchmen of Maine, the disorder and more than 6,000 other rare or "orphan" diseases are receiving increasing attention from government, patient groups, and the pharmaceutical industry.

An orphan disease ...

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